NEWS, REPORTS & POSITION STATEMENTS 1. Infant with rare, incurable disease is first to successfully receive personalized gene therapy treatment In a groundbreaking advance for individualized medicine, an infant diagnosed with carbamoyl phosphate synthetase 1 (CPS1) deficiency— a rare and […]
NEWS, REPORTS & POSITION STATEMENTS 1. EMA’s workplan : ‘Data and AI in medicines regulation to 2028’ EMA and the Heads of Medicines Agencies (HMA) have published a joint workplan “Data and AI in medicines regulation to 2028”. It sets out how […]
NEWS, REPORTS & POSITION STATEMENTS 1. NIH to prioritize human-based research technologies The National Institutes of Health (NIH) is adopting a new initiative to expand innovative, human-based science while reducing animal use in research. Developing and using cutting-edge alternative non-animal […]